Gene Therapy Reverses Effects of Autism-Linked Mutation in Human Brain Organoids - SciTechDaily


5/4/2022 12:00:00 AM2 years 11 months ago

University of California San Diego (UCSD) study uses lab-grown human brain tissue to identify neural abnormalities in Pitt-Hopkins Syndrome and test gene therapy tools. In a study published on May 02, 2022, in the journal Nature Communications, scientists at …

Microscopy images reveal significant differences in size and structure between brain organoids derived from a patient with Pitt-Hopkins Syndrome (right) and from a control (left). Credit: UC San Dieg… [+6824 chars]

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