A Potential Cure for Autism: New Research Finds That Gene Therapy Could Treat Pitt-Hopkins Syndrome - SciTechDaily

New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., finds restoring lost gene activity prevents many disease signs in an animal model of Pitt-Hopkins syndrome, a rare, single-gene neurodevelopmental condition. Pitt-Hopkins syndrome is a r…

A new study has shown that gene therapy may be able to prevent or reverse many deleterious effects of Pitt-Hopkins syndrome New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., f… [+6931 chars]

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