The promising drug duo that may improve spinal muscular atrophy (SMA) treatment - Science Daily

In 2016, Spinraza became the first FDA-approved treatment for spinal muscular atrophy. Researchers have found a way the therapeutic effects of Spinraza may be improved. They discovered that pairing Spinraza with a second FDA-approved drug called valproic acid…

In 2016, Spinraza® became a game-changer for spinal muscular atrophy (SMA) patients. It was the first FDA-approved treatment for the neurodegenerative disease, which is the leading genetic cause of i… [+2006 chars]

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