Phase 1–2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B | NEJM - nejm.org

Original Article from The New England Journal of Medicine — Phase 1–2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B

From the Katharine Dormandy Haemophilia and Thrombosis Centre (P.C., M.P., A.R., M.R.P., E.T., A.N.), Health Services Laboratory, Sonic Healthcare (A.R.), and the Department of Hepatology and Liver T… [+874 chars]

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