Complexities With SMN2 Copies in Spinal Muscular Atrophy: Basil Darras, MD - Neurology Live

The associate neurologist-in-chief at Boston Children’s Hospital discussed the 4-copy conundrum and whether treatment decisions differ based on SMN2 copies for patients with spinal muscular atrophy. [WATCH TIME: 2 minutes]

WATCH TIME: 2 minutes "There was a committee convened by Cure SMA which has met a few times. During the last meeting, we voted in favor of treating babies with 4 copies of SMN2. That was published i… [+1655 chars]

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